Tag: gene_therapy
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FDA Investigating Serious Risk of Malignancy Linked to Zolgensma Gene Therapy
FDA says postmarketing reports link Zolgensma to malignancies, including confirmed insertional oncogenesis involving the GLI1 gene, and warns the risk applies to Itvisma as well.
HealthScience & TechnologyPolitics and GovernmentMedical ScienceFederal GovernmentLegal ZolgensmaItvismaFood and Drug Administrationinsertional oncogenesisspinal muscular atrophygene therapyNovartisFood RecallsFDADrugs
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Penn Medicine Combines CRISPR and Lipid Nanoparticles to Target Duchenne Muscular Dystrophy
Penn Medicine researchers say a system pairing CRISPR gene editing with lipid nanoparticle delivery could halt or even reverse Duchenne muscular dystrophy progression, according to work led by Tejvir S. Khurana.
HealthScience & TechnologyEducationMedical ScienceSocial IssuesLegal Duchenne muscular dystrophyCRISPR gene editinglipid nanoparticlesPenn MedicineTejvir S. KhuranaUniversity of Pennsylvaniagene therapy
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Harvard Gazette Highlights Gene Therapy, Algorithms, and Migraine Research
Harvard Gazette spotlights gene therapy's promise and ethics with David Liu and Eliot Shearer, a podcast on algorithmic feeds, and a researcher's quest to crack the migraine puzzle.
HealthScience & TechnologyPolitics and GovernmentMediaMedical ScienceComputers and InternetArtificial IntelligenceEducationEurope Gene TherapyHarvard GazetteDavid LiuEliot ShearerMigrainePedro SánchezHarvard Radcliffe Institute
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Media Monitor: Gene Therapy for Age-Related Vision Loss Enters Human Trials
MIT Technology Review reports on Yuancheng Lu's pioneering gene therapy for age-related vision loss, which restored sight in mice and has now entered human clinical trials for glaucoma.
Science & TechnologyHealthBusinessMedical ScienceEconomyEducation Yuancheng LuGene therapyAge reversalVision lossMacular degenerationGlaucomaLife BiosciencesMIT Technology ReviewMITsciencetechnology
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Media Monitor: Experimental Gene Therapy Shows Promise for Lifelong Cholesterol Control
TIME Health is reporting on new research into an experimental gene therapy that significantly lowered LDL cholesterol, potentially offering a one-time treatment for heart disease risk.
HealthScience & TechnologyMedical Science Gene therapyCholesterolLDL cholesterolHeart diseaseVerve TherapeuticsEli Lilly & Co.TIME Health